Tagged: orphan drugs

Leveling the Playing Field in Orphan Drug Development

Trials of orphan drugs often involve smaller sample sizes. How much smaller? Cut the typical phase 3 sample size by 75% and then, for many orphan trials, cut a lot more. The Evaluate Pharma Orphan Drug Report 2013 provides valuable data on sample size in phase 3 orphan trials. While the median size was >500… Read more »